Tag: Gene Therapy
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Gene therapy
What is gene therapy ? Gene therapy is emerging as a promising treatment option for diseases which don’t have any treatments. There are so many diseases which don’t have any treatment and are caused due to defective gene. For example Duchenne Muscular Dystrophy DMD, where a patient would lose life without any treatment that treat…
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Hemophilia A Gene Therapy
New drug for Hemophilia A Gene Therapy approved by USFDA. US FDA approved Hemophilia A Gene Therapy. Hemophilia is a disease which causes uncontrolled excessive bleeding, due to absence of clotting factors which help in formation of solid clot that prevents excessive bleeding and wound healing. Patients affected with Hemophilia suffer bleeding bruises, bleeding in…
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Duchenne muscular dystrophy gene therapy
Duchenne muscular dystrophy gene therapy approved by USFDA. Yesterday it was a golden day in the medical profession and Bio pharmaceutical development Duchenne muscular dystrophy gene therapy was approved by USFDA. It has provided hope for life to billions of DMD affected children. Untill 22-06-2023 there was no treatment available for Duchenne muscular dystrophy (DMD).…
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Dystrophic Epidermolysis Bullosa Gene therapy
Herpes-simplex virus type 1 (HSV-1) used as vector for carrier for gene. Gene therapy approved by USFDA for treatment of Dystrophic epidermolysis bullosa (DEB) , The butterfly Skin Disease. Have you heard about a disease called butterfly skin disease or dystrophic Epidermolysis Bullosa? Skin of the patients affected with this disease get ruptured at any…
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Live bacteria Virus used for treatment of diseases
Do you know that there are some diseases which can only be treated by injecting live bacteria and virus at the point of disease. Bladder Cancer treatment with live atenuated microorganisms Bacillus Calmette-Guerin (BCG). Gene Therapy assited by live virus vector, Novel Drug Delivery System. One of such disease is bladder cancer which is treated…
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New Drug A Live Virus Carrying Gene, A Gene Therapy approved by USFDA for treatment of Bladder Cancer that is non metastatic and don’t respond to other treatments like BCG
Novel drug Adstiladrin that delivers genes through a live virus vector, approved by USFDA for treatment of non-muscle invasive Bacillus Calmette-Guérin (BCG)-unresponsive bladder cancer. This month the US FDA has approved a novel drug, a gene therapy that makes use of a live virus (vector) which carries the gene and delivers it to the point…
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USFDA approves first Gene Therapy Drug for Hemophilia B
What is Hemophilia B ? Patients affected with Hemophilia B suffer uncontrolled bleeding from any part of body from inside or from any damaged or wounded body part, some times without any bruise or any cut bleeding occurs from internal organs or oral cavity. Symptoms of Hemophilia B Patients affected with Hemophilia B suffer bleeding…
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